rare diseases

Photo

Ultragenyx Opens Gene Therapy Manufacturing Plant

US biopharma Ultragenyx Pharmaceutical has opened a gene therapy manufacturing facility in Bedford, Massachusetts, USA. The company said it is one of the first in the US with complete end-to-end gene therapy capabilities, from R&D through to therapeutic production at scale.

Photo

Sweden’s Sobi Agrees Merger with CTI BioPharma

Swedish Orphan Biovitrum (Sobi) has agreed a merger with CTI BioPharma, a US biopharmaceutical company focused on blood-related cancers and rare diseases. Through a wholly owned, indirect subsidiary, Sobi plans to commence a cash tender offer that values CTI at $1.7 billion.

Photo

Chiesi Closes Amryt Acquisition

Italian biopharma Chiesi has completed its acquisition of Irish rare disease drugmaker Amryt Pharma. The deal, which was originally announced in January, could be worth up to €1.4 billion for Amryt if certain milestones are met for its epidermolysis bullosa (EB) drug Filsuvez.

Photo

Amgen Boosts Rare Diseases with Horizon Buy

Amgen has agreed to buy Horizon Therapeutics for $28.3 billion including debt, boosting its portfolio of drugs for rare autoimmune and inflammatory diseases and beating rivals Sanofi and Johnson & Johnson, as well as a fourth unnamed company.

Photo

Evotec Enhances Rare Disease Focus with Central Glass Buy

German CDMO Evotec is to acquire compatriot company Central Glass Germany from Japanese owner Central Glass for a nominal price of €1. The transaction, which remains subject to the usual closing conditions, is expected to complete on Nov. 1.

Interview

Leading Transformation
The Path to Sustainable Growth

Leading Transformation

As Executive Vice President of International Chemicals since early 2024, Antje Gerber has been steering Sasol through a pivotal reset—focused on resilience, innovation, and bold sustainability goals.