Keyword: orphan diseases

News

Alexion Valuation Could Choke Any Roche Bid

15.07.2013 - Buying Alexion Pharmaceuticals would help Roche make a splash in the newly lucrative area of rare or so-called orphan diseases, but it could command a price that the Swiss...

News

BioMarin Won't Sell Itself for 25-30% Premium

09.01.2013 - BioMarin Pharmaceutical, which makes high-priced drugs used to treat rare diseases, would not consider a buy-out offer for even a 25-30% premium, according to the company's chief...

News

Top-Selling Drugs for Ultra-Rare Diseases

03.01.2013 - Rare diseases are a growing focus for drug companies, with prices for some treatments for ultra-rare conditions running into hundreds of thousands of dollars a year. The following...

News

Entering the Age of the $1 Million Medicine

03.01.2013 - The Western world's first drug to fix faulty genes promises to transform the lives of patients with an ultra-rare disease that clogs their blood with fat. The only snag is the...